This protocol addresses pulmonary arterial hypertension in patients who have tested negative on acute pulmonary vasoreactivity testing and carry a diagnosis of idiopathic, heritable, or drug-associated PAH, or PAH associated with connective tissue disease (PAH-CTD). It is designed for those who are free of cardiopulmonary comorbidities and are assessed at low or intermediate risk of death.
Drug treatment targets non-vasoreactive patients with IPAH, HPAH, or DPAH, and those with PAH associated with connective tissue disease, who have a negative acute vasoreactivity result and no cardiopulmonary comorbidities at presentation.
For patients at low or intermediate risk in this setting, initial oral combination therapy involving an endothelin receptor antagonist together with a phosphodiesterase-5 inhibitor is recommended. The specific agents, sequencing, monitoring intervals, and escalation criteria are set out in the full structured protocol.
The aim is to achieve and maintain a low-risk profile on optimised medical therapy. Risk status is assessed using WHO functional class, six-minute walk distance, and BNP/NT-proBNP levels. Patients who reach and sustain low-risk status continue on their established regimen.
DOI: 10.1093/eurheartj/ehac237
This section describes drug treatment and is focused on non-vasoreactive patients with IPAH/HPAH/DPAH and on patients with PAH associated with connective tissue disease (PAH-CTD).
For patients presenting at low or intermediate risk, initial combination therapy with an ERA and a PDE5i is recommended.
Cardiopulmonary comorbidities are conditions associated with an increased risk of left ventricular diastolic dysfunction, and include obesity, hypertension, diabetes mellitus, and coronary heart disease; pulmonary comorbidities may include signs of mild parenchymal lung disease and are often associated with a low DLCO (<45% of the predicted value).
Achieving and maintaining a low-risk profile on optimized medical therapy is recommended as a treatment goal in patients with PAH. In patients who achieve a low-risk status with their initial PAH therapy, continuation of treatment is recommended.
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