In patients with hereditary hemochromatosis (HH) who also have severe anemia or congestive heart failure, the standard approach to iron removal may itself carry a significant risk of harm, requiring a distinct therapeutic strategy.
Phlebotomy is the conventional first step in managing systemic iron overload in HH. However, when a patient presents with severe anemia or congestive heart failure, phlebotomy carries the potential to worsen their condition. In this setting — or when a patient is intolerant or refractory to phlebotomy — an alternative iron-reduction strategy is strongly indicated.
The primary therapeutic targets are meaningful reduction in serum ferritin levels and hepatic iron concentration, assessed over the course of treatment.
DOI: 10.14309/ajg.0000000000000315
We recommend the use of iron chelation for the treatment of HH for the patient who is intolerant or refractory to phlebotomy or when phlebotomy has the potential for harm, such as in patients with severe anemia or congestive heart failure (strong recommendation, low quality of evidence).
After 12 months of treatment, deferasirox achieved reduction in median ferritin levels and HIC and was well tolerated (148).
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