Treatment of Chronic Granulomatous Disease When Haematopoietic Stem Cell Transplantation Is Being Considered
This protocol addresses the management of patients with confirmed chronic granulomatous disease (CGD) who are being evaluated as candidates for haematopoietic stem cell transplantation.
Clinical scenario
The patient has a confirmed diagnosis of chronic granulomatous disorder and is under consideration for haematopoietic stem cell transplantation (HSCT).
Treatment goals
The primary clinical objectives are resolution of infection and colitis.
Approach — partial overview
When HSCT is pursued, donor selection and conditioning follow established international guidelines — the full protocol specifies the donor criteria and conditioning approach in detail.
Complete regimen, eligibility criteria, and conditioning details available in the full protocol ↓
References
Haematopoietic stem cell transplantation (HSCT) can cure CGD, with resolution of infection and colitis.
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